Ultra Market Research | Global Sickle Cell Disease Treatment Market
Global Sickle Cell Disease Treatment Market
Report ID : 870
Category : Pharmaceuticals,Global
No Of Pages : `188
Published on: November 2024
Status: Published
Format :
Key Question Answer
Global Market Outlook
In-depth analysis of global and regional trends
Analyze and identify the major players in the market, their market share, key developments, etc.
To understand the capability of the major players based on products offered, financials, and strategies.
Identify disrupting products, companies, and trends.
To identify opportunities in the market.
Analyze the regional penetration of players, products, and services in the market.
Comparison of major players financial performance.
Evaluate strategies adopted by major players.
Recommendations
Global Sickle Cell Disease Treatment Market
Introduction
The global sickle cell disease treatment market addresses the therapeutic and management needs of sickle cell anemia, a hereditary blood disorder characterized by abnormal hemoglobin that leads to rigid, sickle-shaped red blood cells. The disease causes severe pain, anemia, and organ damage, significantly affecting quality of life. Rising awareness, advancements in gene therapy, and innovative drug development have fueled the market's growth. The market is witnessing increasing investments in curative treatments like hematopoietic stem cell transplantation and gene-editing technologies. In 2023, the sickle cell disease drugs market was valued at approximately $5 billion, with projections for robust growth driven by the expanding adoption of disease-modifying therapies and innovative treatments across the globe.
Segmentation
By Therapeutics
Disease-Modifying Drugs
Hydroxyurea
L-glutamine
Others
Gene Therapies
CRISPR-Cas9 Therapies
Lentiviral Vector Therapies
Curative Therapies
Hematopoietic Stem Cell Transplantation
Bone Marrow Transplants
By Diagnostics
Screening Tests
Newborn Screening
Prenatal Testing
Blood Tests
Imaging Techniques
Doppler Ultrasound
Magnetic Resonance Imaging (MRI)
Others
By End-Users
Hospitals
Specialty Care Centers
Emergency Departments
Clinics
Hematology Clinics
Genetic Counseling Centers
Research Institutes
Academic Research Labs
Clinical Trial Centers
By Distribution Channels
Hospital Pharmacies
Inpatient Pharmacies
Specialty Pharmacies
Retail Pharmacies
Chain Pharmacies
Standalone Pharmacies
Online Pharmacies
By Geography
North America United States Canada
Europe Germany France United Kingdom
Rest of Europe
Asia Pacific China Japan India
Southeast Asia Rest of Asia Pacific
Latin America Brazil Rest of Latin America
Middle East & Africa (MEA) GCC North Africa South Africa Rest of Middle East & Africa
List of Market Players
Novartis AG (Switzerland)
Global Blood Therapeutics (United States)
Vertex Pharmaceuticals (United States)
Editas Medicine (United States)
CRISPR Therapeutics (Switzerland)
Sangamo Therapeutics (United States)
bluebird bio (United States)
Pfizer Inc. (United States)
Sanofi (France)
Bioverativ (United States)
Emmaus Life Sciences (United States)
Acceleron Pharma (United States)
Editas Medicine (United States)
Merck & Co. (United States)
Celgene Corporation (United States)
Drivers
The global sickle cell disease treatment market is propelled by advancements in gene therapy and disease-modifying drugs. Increasing global prevalence of sickle cell disease, particularly in Africa, India, and the Middle East, has intensified the demand for effective treatment solutions. Rising healthcare awareness and enhanced government support for rare disease management drive the adoption of advanced diagnostic and therapeutic approaches. Technological innovations, such as CRISPR gene editing, offer promising curative potential, further expanding the market. Additionally, patient advocacy groups and growing accessibility to new drugs contribute significantly to market growth.
Restraints
Despite advancements, the sickle cell disease drugs market faces challenges such as high treatment costs and limited availability of curative therapies. In low-income regions, inadequate healthcare infrastructure and restricted access to specialized care hinder the market's reach. Regulatory hurdles for gene therapies and lengthy approval processes slow down the introduction of innovative treatments. Moreover, a lack of awareness among healthcare providers in certain regions leads to underdiagnosis and delayed interventions, impeding market growth.
Opportunity
The growing focus on personalized medicine and innovative technologies offers substantial growth opportunities in the global SCD market. Emerging markets in Asia-Pacific and Africa, with high disease prevalence, present untapped potential for market players. Increasing investment in research and development for advanced therapies, such as lentiviral gene therapies, could address unmet needs. Collaborations between pharmaceutical companies and non-profit organizations can enhance accessibility to affordable treatments, particularly in underserved regions. Expanding newborn screening programs globally provides early diagnosis, paving the way for timely interventions and market growth.
Trend
The sickle cell disease management market is witnessing trends such as the rise of gene-editing technologies like CRISPR and the development of targeted therapies. Integration of artificial intelligence (AI) in diagnostics improves the precision and efficiency of disease detection. Wearable devices for remote monitoring of symptoms are gaining popularity, enabling better disease management. Partnerships between biotech firms and academic institutions drive innovation, while patient-centric care models and holistic management strategies become focal points.
Hydroxyurea, gene-editing therapies, and hematopoietic stem cell transplants are key options.
High treatment costs, limited infrastructure in low-income regions, and regulatory hurdles.
Novartis, Global Blood Therapeutics, Vertex Pharmaceuticals, and CRISPR Therapeutics.
Gene-editing advancements, wearable health monitoring, and AI-integrated diagnostics.
1. Introduction 1.1 Report Description 1.2 Research Methodology 1.2.1 Data Mining 1.2.2 Market Modeling and Forecasting 1.2.3 Data Validation 1.2.4 Industry Analysis 2. Market Dashboard 3. Market Overview 3.1 Market Definition and Scope 3.2 Market Segmentation 3.2.1 By Therapeutics 3.2.2 By Diagnostics 3.2.3 By End-Users 3.2.4 By Distribution Channels 3.3 Market Dynamics 3.3.1 Drivers 3.3.2 Restraints 3.3.3 Opportunities 3.3.4 Challenges 4. Global Sickle Cell Disease Treatment Market by Therapeutics 4.1 Introduction 4.2 Market Size and Growth Rate by Therapeutics (2024-2030) 4.2.1 Disease-Modifying Drugs 4.2.1.1 Hydroxyurea 4.2.1.2 L-glutamine 4.2.1.3 Others 4.2.2 Gene Therapies 4.2.2.1 CRISPR-Cas9 Therapies 4.2.2.2 Lentiviral Vector Therapies 4.2.3 Curative Therapies 4.2.3.1 Hematopoietic Stem Cell Transplantation 4.2.3.2 Bone Marrow Transplants 5. Global Sickle Cell Disease Treatment Market by Diagnostics 5.1 Introduction 5.2 Market Size and Growth Rate by Diagnostics (2024-2030) 5.2.1 Screening Tests 5.2.1.1 Newborn Screening 5.2.1.2 Prenatal Testing 5.2.1.3 Blood Tests 5.2.2 Imaging Techniques 5.2.2.1 Doppler Ultrasound 5.2.2.2 Magnetic Resonance Imaging (MRI) 5.2.2.3 Others 6. Global Sickle Cell Disease Treatment Market by End-Users 6.1 Introduction 6.2 Market Size and Growth Rate by End-Users (2024-2030) 6.2.1 Hospitals 6.2.1.1 Specialty Care Centers 6.2.1.2 Emergency Departments 6.2.2 Clinics 6.2.2.1 Hematology Clinics 6.2.2.2 Genetic Counseling Centers 6.2.3 Research Institutes 6.2.3.1 Academic Research Labs 6.2.3.2 Clinical Trial Centers 7. Global Sickle Cell Disease Treatment Market by Distribution Channels 7.1 Introduction 7.2 Market Size and Growth Rate by Distribution Channels (2024-2030) 7.2.1 Hospital Pharmacies 7.2.1.1 Inpatient Pharmacies 7.2.1.2 Specialty Pharmacies 7.2.2 Retail Pharmacies 7.2.2.1 Chain Pharmacies 7.2.2.2 Standalone Pharmacies 7.2.3 Online Pharmacies 8. Competitive Landscape 8.1 Company Profiles 8.1.1 Novartis AG (Switzerland) • Business Overview • Product Portfolio • Strategic Developments • Financial Overview 8.1.2 Global Blood Therapeutics (United States) • Business Overview • Product Portfolio • Strategic Developments • Financial Overview 8.1.3 Vertex Pharmaceuticals (United States) • Business Overview • Product Portfolio • Strategic Developments • Financial Overview 8.1.4 Editas Medicine (United States) • Business Overview • Product Portfolio • Strategic Developments • Financial Overview 8.1.5 CRISPR Therapeutics (Switzerland) • Business Overview • Product Portfolio • Strategic Developments • Financial Overview 8.1.6 Sangamo Therapeutics (United States) • Business Overview • Product Portfolio • Strategic Developments • Financial Overview 8.1.7 bluebird bio (United States) • Business Overview • Product Portfolio • Strategic Developments • Financial Overview 8.1.8 Pfizer Inc. (United States) • Business Overview • Product Portfolio • Strategic Developments • Financial Overview 8.1.9 Sanofi (France) • Business Overview • Product Portfolio • Strategic Developments • Financial Overview 8.1.10 Bioverativ (United States) • Business Overview • Product Portfolio • Strategic Developments • Financial Overview 8.1.11 Emmaus Life Sciences (United States) • Business Overview • Product Portfolio • Strategic Developments • Financial Overview 8.1.12 Acceleron Pharma (United States) • Business Overview • Product Portfolio • Strategic Developments • Financial Overview 8.1.13 Merck & Co. (United States) • Business Overview • Product Portfolio • Strategic Developments • Financial Overview 8.1.14 Celgene Corporation (United States) • Business Overview • Product Portfolio • Strategic Developments • Financial Overview
11. List of Tables and Figure Table Global Sickle Cell Disease Treatment Market Size by Therapeutics (2024-2030) Table Disease-Modifying Drugs Market Size by Sub-type (2024-2030) Table Gene Therapies Market Size by Sub-type (2024-2030) Table Curative Therapies Market Size by Sub-type (2024-2030) Table Global Sickle Cell Disease Treatment Market Size by Diagnostics (2024-2030) Table Screening Tests Market Size by Sub-type (2024-2030) Table Imaging Techniques Market Size by Sub-type (2024-2030) Table Global Sickle Cell Disease Treatment Market Size by End-Users (2024-2030) Table Hospitals Market Size by Sub-type (2024-2030) Table Clinics Market Size by Sub-type (2024-2030) Table Research Institutes Market Size by Sub-type (2024-2030) Table Global Sickle Cell Disease Treatment Market Size by Distribution Channels (2024-2030) Table Hospital Pharmacies Market Size by Sub-type (2024-2030) Table Retail Pharmacies Market Size by Sub-type (2024-2030) List of Figures Figure Global Sickle Cell Disease Treatment Market Size and Growth Rate by Therapeutics (2024-2030) Figure Disease-Modifying Drugs Market Growth Rate by Sub-type (2024-2030) Figure Gene Therapies Market Growth Rate by Sub-type (2024-2030) Figure Curative Therapies Market Growth Rate by Sub-type (2024-2030) Figure Global Sickle Cell Disease Treatment Market Size and Growth Rate by Diagnostics (2024-2030) Figure Screening Tests Market Growth Rate by Sub-type (2024-2030) Figure Imaging Techniques Market Growth Rate by Sub-type (2024-2030) Figure Global Sickle Cell Disease Treatment Market Size and Growth Rate by End-Users (2024-2030) Figure Global Sickle Cell Disease Treatment Market Size and Growth Rate by Distribution Channels (2024-2030) Table Global Sickle Cell Disease Treatment Market by Regions (2021-2023) Table Global Sickle Cell Disease Treatment Market by Regions (2023-2030) Figure North America Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table North America Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table North America Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table North America Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table North America Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table North America Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table North America Global Sickle Cell Disease Treatment Market by End User (2023-2030) Table North America Global Sickle Cell Disease Treatment Market by Country (2021-2023) Table North America Global Sickle Cell Disease Treatment Market by Country (2023-2030) Figure United States Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table United States Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table United States Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table United States Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table United States Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table United States Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table United States Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure Canada Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Canada Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Canada Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Canada Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Canada Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Canada Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Canada Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure Europe Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Europe Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Europe Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Europe Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Europe Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Europe Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Europe Global Sickle Cell Disease Treatment Market by End User (2023-2030) Table Europe Global Sickle Cell Disease Treatment Market by Country (2021-2023) Table Europe Global Sickle Cell Disease Treatment Market by Country (2023-2030) Figure Germany Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Germany Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Germany Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Germany Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Germany Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Germany Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Germany Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure France Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table France Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table France Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table France Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table France Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table France Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table France Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure United Kingdom UK Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table United Kingdom UK Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table United Kingdom UK Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table United Kingdom UK Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table United Kingdom UK Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table United Kingdom UK Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table United Kingdom UK Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure Russia Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Russia Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Russia Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Russia Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Russia Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Russia Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Russia Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure Italy Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Italy Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Italy Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Italy Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Italy Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Italy Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Italy Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure Rest of Europe Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Rest of Europe Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Rest of Europe Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Rest of Europe Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Rest of Europe Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Rest of Europe Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Rest of Europe Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure Asia-Pacific Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Asia-Pacific Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Asia-Pacific Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Asia-Pacific Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Asia-Pacific Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Asia-Pacific Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Asia-Pacific Global Sickle Cell Disease Treatment Market by End User (2023-2030) Table Asia-Pacific Global Sickle Cell Disease Treatment Market by Country (2021-2023) Table Asia-Pacific Global Sickle Cell Disease Treatment Market by Country (2023-2030) Figure China Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table China Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table China Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table China Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table China Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table China Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table China Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure Japan Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Japan Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Japan Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Japan Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Japan Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Japan Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Japan Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure Korea Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Korea Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Korea Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Korea Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Korea Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Korea Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Korea Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure India Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table India Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table India Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table India Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table India Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table India Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table India Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure Southeast Asia Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Southeast Asia Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Southeast Asia Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Southeast Asia Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Southeast Asia Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Southeast Asia Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Southeast Asia Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure Rest of Asia-Pacific Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Rest of Asia-Pacific Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Rest of Asia-Pacific Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Rest of Asia-Pacific Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Rest of Asia-Pacific Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Rest of Asia-Pacific Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Rest of Asia-Pacific Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure Latin America Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Latin America Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Latin America Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Latin America Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Latin America Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Latin America Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Latin America Global Sickle Cell Disease Treatment Market by End User (2023-2030) Table Latin America Global Sickle Cell Disease Treatment Market by Country (2021-2023) Table Latin America Global Sickle Cell Disease Treatment Market by Country (2023-2030) Figure Brazil Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Brazil Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Brazil Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Brazil Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Brazil Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Brazil Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Brazil Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure Mexico Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Mexico Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Mexico Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Mexico Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Mexico Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Mexico Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Mexico Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure Columbia Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Columbia Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Columbia Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Columbia Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Columbia Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Columbia Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Columbia Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure Rest of Latin America Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Rest of Latin America Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Rest of Latin America Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Rest of Latin America Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Rest of Latin America Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Rest of Latin America Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Rest of Latin America Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure Middle East and Africa Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Middle East and Africa Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Middle East and Africa Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Middle East and Africa Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Middle East and Africa Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Middle East and Africa Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Middle East and Africa Global Sickle Cell Disease Treatment Market by End User (2023-2030) Table Middle East and Africa Global Sickle Cell Disease Treatment Market by Country (2021-2023) Table Middle East and Africa Global Sickle Cell Disease Treatment Market by Country (2023-2030) Figure Saudi Arabia Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Saudi Arabia Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Saudi Arabia Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Saudi Arabia Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Saudi Arabia Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Saudi Arabia Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Saudi Arabia Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure United Arab Emirates Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table United Arab Emirates Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table United Arab Emirates Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table United Arab Emirates Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table United Arab Emirates Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table United Arab Emirates Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table United Arab Emirates Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure South Africa Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table South Africa Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table South Africa Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table South Africa Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table South Africa Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table South Africa Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table South Africa Global Sickle Cell Disease Treatment Market by End User (2023-2030) Figure Rest of Middle East and Africa Global Sickle Cell Disease Treatment Market Size and Growth Rate (2021-2030) Table Rest of Middle East and Africa Global Sickle Cell Disease Treatment Market by Therapeutic (2021-2023) Table Rest of Middle East and Africa Global Sickle Cell Disease Treatment Market by Therapeutic (2023-2030) Table Rest of Middle East and Africa Global Sickle Cell Disease Treatment Market by Diagnostic(2021-2023) Table Rest of Middle East and Africa Global Sickle Cell Disease Treatment Market by Diagnostic(2023-2030) Table Rest of Middle East and Africa Global Sickle Cell Disease Treatment Market by End User (2021-2023) Table Rest of Middle East and Africa Global Sickle Cell Disease Treatment Market by End User (2023-2030) Tables Financial Overview of Key Companies Table Novartis AG Sickle Cell Disease Treatment Financial Overview Table Global Blood Therapeutics Sickle Cell Disease Treatment Financial Overview Table Vertex Pharmaceuticals Sickle Cell Disease Treatment Financial Overview Table Editas Medicine Sickle Cell Disease Treatment Financial Overview Table CRISPR Therapeutics Sickle Cell Disease Treatment Financial Overview Table Sangamo Therapeutics Sickle Cell Disease Treatment Financial Overview Table bluebird bio Sickle Cell Disease Treatment Financial Overview Table Pfizer Inc. Sickle Cell Disease Treatment Financial Overview Table Sanofi Sickle Cell Disease Treatment Financial Overview Table Bioverativ Sickle Cell Disease Treatment Financial Overview Table Emmaus Life Sciences Sickle Cell Disease Treatment Financial Overview Table Acceleron Pharma Sickle Cell Disease Treatment Financial Overview Table Merck & Co. Sickle Cell Disease Treatment Financial Overview Table Celgene Corporation Sickle Cell Disease Treatment Financial Overview
Research Methodology
The process of market research at Ultra Market Research is an iterative in application and usually follows following path. Information from secondary used to build data models, then results from data models are validated from primary participants. Then cycle repeats where, according to inputs from primary participants, additional secondary research is done and new Information is again incorporated into data model. The process continues till desired level of Information is not generated
To calculate the market size, the report considers the revenue generated from the sales of Ultra Market Research providers. The revenue generated from the sales of Ultra Market Research has been calculated through primary and secondary research. The report also presents the key players operating in the Ultra Market Research market across the globe identified through secondary research and a corresponding detailed analysis of the top vendors in the market. The market size calculation also includes distribution channel segmentation determined using secondary sources and verified through primary sources.
Secondary Research
The secondary research source that are typically referred to include, but are not limited to:
Company websites, annual reports, financial reports, broker reports, investor presentations and SEC filings
Internal and external proprietary databases, relevant patent and regulatory databases
National government documents, statistical databases and market reports
News articles, press releases and web-casts specific to the companies operating in the market
The source for secondary research includes but is not limited to: Factiva, Hoovers and Statista
Inner Circle Represents – Stage of Research Process
Middle Circle Represents – Source of Information
Outer Circle Represents – Information Derived from that source
Primary Research We conduct primary interviews on an ongoing basis with industry participants and commentators in order to validate data and analysis. A typical research interview fulfills the following functions:
It provides first-hand Information on the market size, market trends, growth trends, competitive landscape, future outlook etc.
Helps in validating and strengthening the secondary research findings
Further develops the analysis team’s expertise and market understanding
Primary research involves E-mail interactions, telephonic interviews as well as face-to-face interviews for each market, category, segment and sub-segment across geographies
The participants who typically take part in such a process include, but are not limited to:
Industry participants: CEOs, VPs, marketing/ distribution channel managers, market intelligence managers and national sales managers
Purchasing managers, technical personnel, distributors and resellers
Outside experts: Investment bankers, valuation experts, research analysts specializing in specific markets
Key opinion leaders specializing in different areas corresponding to different industry distribution channels
Models Where no hard data is available, we use modeling and estimates in order to produce comprehensive data sets. A rigorous methodology is adopted in which the available hard data is cross referenced with the following data distribution channels to produce estimates:
Demographic data: Population split by segment
Macro-economic indicators: GDP, etc.
Industry indicators: Expenditure, distribution channel stage & infrastructure, sector growth and facilities.
Data is then cross checked by the expert panel.
2..1 Company Share Analysis Model
Company share analysis is used to derive the size of Global market. As well as study of revenues of companies for last three to five years also provide the base for forecasting the market size and its growth rate. This model is built in following steps: 2..2 Revenue Based Modeling
Revenue based models can be built in two ways – Top-Down or Bottom-Up irrespective of industry. Market size estimated from company share analysis acts as a validation point for bottom-up approach where as it acts as starting point for top-down approach.
2.1 Research Limitations Inflation is not a part of pricing in this report. Prices of Global Sickle Cell Disease Treatment Market and its derivatives vary in each region and hence similar revenue ratio does not follow for each individual region. The same price for each distribution channel has been taken into account while estimating and forecasting market revenue Globally. Regional average price has been considered while breaking down this market by application in each region. This report provides market size of Global Sickle Cell Disease Treatment Market for the past year and forecasts for the next six years. Global Sickle Cell Disease Treatment Market. Market size is given in terms of revenue. Market revenue is defined in USD Million. Market numbers are given on the basis of different Global Sickle Cell Disease Treatment Market categories. Market size and forecasts for each major application is provided in the context of Global market. The numbers provided in this report are derived on the basis of demand for Global Sickle Cell Disease Treatment Market from different application industries in different regions.
Segmentation
By Therapeutics
Disease-Modifying Drugs
Hydroxyurea
L-glutamine
Others
Gene Therapies
CRISPR-Cas9 Therapies
Lentiviral Vector Therapies
Curative Therapies
Hematopoietic Stem Cell Transplantation
Bone Marrow Transplants
By Diagnostics
Screening Tests
Newborn Screening
Prenatal Testing
Blood Tests
Imaging Techniques
Doppler Ultrasound
Magnetic Resonance Imaging (MRI)
Others
By End-Users
Hospitals
Specialty Care Centers
Emergency Departments
Clinics
Hematology Clinics
Genetic Counseling Centers
Research Institutes
Academic Research Labs
Clinical Trial Centers
By Distribution Channels
Hospital Pharmacies
Inpatient Pharmacies
Specialty Pharmacies
Retail Pharmacies
Chain Pharmacies
Standalone Pharmacies
Online Pharmacies
By Geography
North America United States Canada
Europe Germany France United Kingdom
Rest of Europe
Asia Pacific China Japan India
Southeast Asia Rest of Asia Pacific
Latin America Brazil Rest of Latin America
Middle East & Africa (MEA) GCC North Africa South Africa Rest of Middle East & Africa